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RNA-Targeting Discovery Platform for Neuro Indications
Machine Learning & Artificial Intelligence
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We are harnessing novel bioinformatics and machine learning techniques to build predictive oligonucleotide therapeutic tools and expand the therapeutic target space.
Screening Technology
Our wet lab is leveraging robotics and automation to perform high-throughput screening of ASO therapeutics for potency and selectivity.
RNA Splicing Platform
LJSplice is a new industry leading software that provides scientists with an unparalleled view of RNA binding proteins for designing efficient and targeted splicing strategies on any gene.
Our Partners
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Contact Us
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